A key GM1 challenge, among many, is the ability to treat patients with medicine or gene therapy intravenously. The blood-brain barrier in effect prevents the treatment from reaching the brain. Canadian medical "researchers have unlocked a non-invasive way to deliver medication deep into the brain, opening the door to better treatments for brain tumours, Alzheimer's, Parkinson's and more."
News like this gives GM1 families hope. Read more in the two articles below:
http://www.inquisitr.com/2552192/canadian-doctor-first-to-break-blood-brain-barrier/